New approaches in management and treatment of primary immunodeficiencies and other genetic diseases.

During my PhD program in "Human Reproduction, Development and Growth" (XXVII Cycle, years 2011-2014), I contributed to the development of new approaches for the treatment of PIDs and other genetic diseases by advanced therapies, such as gene and cellular therapy. Moreover, I participated in the clinical and biological characterization of patients with immunodeficiencies and in the implementation of new approaches for the clinical management of children affected by hematological and immunological disorders undergoing bone marrow transplantation. My other lines of research have been focused on the use of new drugs in pediatric population, characterization of severe and unusual conditions and description of the State of the Art of known patologies in childhood.