Sfoglia per Corso Immunologia, medicina molecolare e biotecnologie applicate
Mostrati risultati da 1 a 3 di 3
Long term follow-up of pediatric patients affected by Hurler syndrome enrolled in a phase I/II ex-vivo gene therapy clinical trial and development of a novel ex-vivo gene therapy platform to treat lysosomal storage diseases
2024
Novel gene editing techniques for hematological pediatric diseases. Project 1: base editing approaches for the treatment of β-thalassemia. Project 2: pediatric SAMD9/SAMD9L-myelodysplasia: a base-editing approach
2024
Regulatory dendritic cells in celiac disease: biology and potential cell-based approaches
2022
| Istituto | Anno di pubblicazione | Titolo | Autore | file(s) |
|---|---|---|---|---|
| Università degli Studi di Roma Tor Vergata | 2024 | Long term follow-up of pediatric patients affected by Hurler syndrome enrolled in a phase I/II ex-vivo gene therapy clinical trial and development of a novel ex-vivo gene therapy platform to treat lysosomal storage diseases | - | |
| Università degli Studi di Roma Tor Vergata | 2024 | Novel gene editing techniques for hematological pediatric diseases. Project 1: base editing approaches for the treatment of β-thalassemia. Project 2: pediatric SAMD9/SAMD9L-myelodysplasia: a base-editing approach | - | |
| Università degli Studi di Roma Tor Vergata | 2022 | Regulatory dendritic cells in celiac disease: biology and potential cell-based approaches | - |
Mostrati risultati da 1 a 3 di 3
Legenda icone
- file ad accesso aperto
- file disponibili sulla rete interna
- file disponibili agli utenti autorizzati
- file disponibili solo agli amministratori
- file sotto embargo
- nessun file disponibile